Gene Therapy for Fibrodysplasia Ossificans Progressiva: Feasibility and Obstacles

Fibrodysplasia ossificans progressiva (FOP) is a rare and devastating genetic disease, in which soft connective tissue is converted into heterotopic bone through an endochondral ossification process. Patients succumb early as they gradually become trapped in a second skeleton of heterotopic bone. Al...

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Detalles Bibliográficos
Autores principales: Eekhoff, Elisabeth M.W., de Ruiter, Ruben D., Smilde, Bernard J., Schoenmaker, Ton, de Vries, Teun J., Netelenbos, Coen, Hsiao, Edward C., Scott, Christiaan, Haga, Nobuhiko, Grunwald, Zvi, De Cunto, Carmen L., di Rocco, Maja, Delai, Patricia L. R., Diecidue, Robert J., Madhuri, Vrisha, Cho, Tae-Joon, Morhart, Rolf, Friedman, Clive S., Zasloff, Michael, Pals, Gerard, Shim, Jae-Hyuck, Gao, Guangping, Kaplan, Frederick, Pignolo, Robert J., Micha, Dimitra
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Mary Ann Liebert, Inc., publishers 2022
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9419966/
https://www.ncbi.nlm.nih.gov/pubmed/35502479
http://dx.doi.org/10.1089/hum.2022.023

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9419966/
https://www.ncbi.nlm.nih.gov/pubmed/35502479
http://dx.doi.org/10.1089/hum.2022.023

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