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Efficacy of CRISPR-Based Gene Editing in a Sickle Cell Disease Patient as Measured through the Eye

Sickle cell disease (SCD) exists on a phenotypic spectrum with variable genetic expressivity, making it difficult to assess an individual patient's risk of complications at any particular point in time. Current and emerging SCD treatments, including CRISPR-based gene editing, result in a variab...

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Detalles Bibliográficos
Autores principales: Pinhas, Alexander, Zhou, Davis B., Otero-Marquez, Oscar, Castanos Toral, Maria V., Migacz, Justin V., Glassberg, Jeffrey, Rosen, Richard B., Chui, Toco Y. P.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Hindawi 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9424027/
https://www.ncbi.nlm.nih.gov/pubmed/36046774
http://dx.doi.org/10.1155/2022/6079631