Switching between Enzyme Replacement Therapies and Substrate Reduction Therapies in Patients with Gaucher Disease: Data from the Gaucher Outcome Survey (GOS)

Switching between enzyme replacement therapies (ERT) and substrate reduction therapies (SRT) in patients with type 1 Gaucher disease (GD1) is not uncommon; however, the reasons for switchng treatments have not been explored in detail. Data from the Gaucher Outcome Survey (GOS), an international regi...

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Detalles Bibliográficos
Autores principales: Hughes, Derralynn A., Deegan, Patrick, Giraldo, Pilar, Göker-Alpan, Özlem, Lau, Heather, Lukina, Elena, Revel-Vilk, Shoshana, Scarpa, Maurizio, Botha, Jaco, Gadir, Noga, Zimran, Ari
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2022
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9457166/
https://www.ncbi.nlm.nih.gov/pubmed/36079085
http://dx.doi.org/10.3390/jcm11175158

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9457166/
https://www.ncbi.nlm.nih.gov/pubmed/36079085
http://dx.doi.org/10.3390/jcm11175158

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