Gene Therapy and Hemophilia: Where Do We Go from Here?

Gene therapy for hemophilia using adeno-associated virus (AAV) derived vectors can reduce or eliminate patients’ disease-related complications and improve their quality of life. Broad implementation globally will lead to societal gains and foster health equity. Several vector products each for facto...

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Detalles Bibliográficos
Autores principales: Bolous, Nancy S, Bhatt, Nidhi, Bhakta, Nickhill, Neufeld, Ellis J, Davidoff, Andrew M, Reiss, Ulrike M
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Dove 2022
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9550170/
https://www.ncbi.nlm.nih.gov/pubmed/36226233
http://dx.doi.org/10.2147/JBM.S371438

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9550170/
https://www.ncbi.nlm.nih.gov/pubmed/36226233
http://dx.doi.org/10.2147/JBM.S371438

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