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Gene therapy for cystic fibrosis: Challenges and prospects

Cystic fibrosis (CF) is a life-threatening autosomal-recessive disease caused by mutations in a single gene encoding cystic fibrosis transmembrane conductance regulator (CFTR). CF effects multiple organs, and lung disease is the primary cause of mortality. The median age at death from CF is in the e...

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Detalles Bibliográficos
Autores principales: Sui, Hongshu, Xu, Xinghua, Su, Yanping, Gong, Zhaoqing, Yao, Minhua, Liu, Xiaocui, Zhang, Ting, Jiang, Ziyao, Bai, Tianhao, Wang, Junzuo, Zhang, Jingjun, Xu, Changlong, Luo, Mingjiu
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9592762/
https://www.ncbi.nlm.nih.gov/pubmed/36304167
http://dx.doi.org/10.3389/fphar.2022.1015926