CSF IL-8 Associated with Response to Gene Therapy in a Case Series of Spinal Muscular Atrophy

Gene therapies have greatly changed the outlook in spinal muscular atrophy (SMA), and this disorder provides a rare opportunity to study longitudinal biomarker changes correlated with reduced disease burden and improved clinical outcomes. Recent work suggests clinical response to correlate with decl...

Descripción completa

Detalles Bibliográficos
Autores principales: Verma, Sumit, Perry, Kelsey, Razdan, Raj, Howell, J. Christina, Dawson, Alice L., Hu, William T.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer International Publishing 2022
Materias:
Original Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9607706/
https://www.ncbi.nlm.nih.gov/pubmed/36289175
http://dx.doi.org/10.1007/s13311-022-01305-9

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9607706/
https://www.ncbi.nlm.nih.gov/pubmed/36289175
http://dx.doi.org/10.1007/s13311-022-01305-9

Ejemplares similares