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CSF IL-8 Associated with Response to Gene Therapy in a Case Series of Spinal Muscular Atrophy
Gene therapies have greatly changed the outlook in spinal muscular atrophy (SMA), and this disorder provides a rare opportunity to study longitudinal biomarker changes correlated with reduced disease burden and improved clinical outcomes. Recent work suggests clinical response to correlate with decl...
| Autores principales: | , , , , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
Springer International Publishing
2022
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9607706/ https://www.ncbi.nlm.nih.gov/pubmed/36289175 http://dx.doi.org/10.1007/s13311-022-01305-9 |