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Suppression of pullulanase-induced cytotoxic T cell response with a dual promoter in GSD IIIa mice
Glycogen debranching enzyme deficiency in glycogen storage disease type III (GSD III) results in excessive glycogen accumulation in multiple tissues, primarily the liver, heart, and skeletal muscle. We recently reported that an adeno-associated virus vector expressing a bacterial debranching enzyme...
Autores principales: | Lim, Jeong-A, Kishnani, Priya S., Sun, Baodong |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
American Society for Clinical Investigation
2022
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9746900/ https://www.ncbi.nlm.nih.gov/pubmed/36264632 http://dx.doi.org/10.1172/jci.insight.152970 |
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