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In Vivo Hematopoietic Stem Cell Genome Editing: Perspectives and Limitations

The tremendous evolution of genome-editing tools in the last two decades has provided innovative and effective approaches for gene therapy of congenital and acquired diseases. Zinc-finger nucleases (ZFNs), transcription activator- like effector nucleases (TALENs) and CRISPR-Cas9 have been already ap...

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Detalles Bibliográficos
Autores principales:	Psatha, Nikoletta, Paschoudi, Kiriaki, Papadopoulou, Anastasia, Yannaki, Evangelia
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2022
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9778055/ https://www.ncbi.nlm.nih.gov/pubmed/36553489 http://dx.doi.org/10.3390/genes13122222

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