Gene-agnostic therapeutic approaches for inherited retinal degenerations

Inherited retinal diseases (IRDs) are associated with mutations in over 250 genes and represent a major cause of irreversible blindness worldwide. While gene augmentation or gene editing therapies could address the underlying genetic mutations in a small subset of patients, their utility remains lim...

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Detalles Bibliográficos
Autores principales: John, Molly C., Quinn, Joel, Hu, Monica L., Cehajic-Kapetanovic, Jasmina, Xue, Kanmin
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2023
Materias:
Molecular Neuroscience
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9881597/
https://www.ncbi.nlm.nih.gov/pubmed/36710928
http://dx.doi.org/10.3389/fnmol.2022.1068185

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9881597/
https://www.ncbi.nlm.nih.gov/pubmed/36710928
http://dx.doi.org/10.3389/fnmol.2022.1068185

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