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AAV Engineering for Improving Tropism to the Central Nervous System

SIMPLE SUMMARY: Adeno-associated virus (AAV) is a small, non-pathogenic, and replication-defective virus that mainly infects primates. AAV has demonstrated great success in pre-clinical and clinical applications, including central nervous system (CNS), ocular, muscular, and liver diseases. We have e...

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Detalles Bibliográficos
Autores principales: Ghauri, Muhammad S., Ou, Li
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2023
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9953251/
https://www.ncbi.nlm.nih.gov/pubmed/36829465
http://dx.doi.org/10.3390/biology12020186