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Policy for rare diseases

Professor Bobby Gaspar is a distinguished physician-scientist who is a thought leader in translating basic research from bench-to-bedside and strategic work that facilitated bringing life-saving therapies to patients with rare diseases. He has over 30 years of experience in pediatric medicine workin...

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Detalles Bibliográficos
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Nature Publishing Group UK 2023
Materias:
Q&A
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9974947/
https://www.ncbi.nlm.nih.gov/pubmed/36854888
http://dx.doi.org/10.1038/s43856-023-00254-4