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Long-term follow-up of renal function in patients treated with migalastat for Fabry disease

The effect of migalastat on long-term renal outcomes in enzyme replacement therapy (ERT)–naive and ERT-experienced patients with Fabry disease is not well defined. An integrated posthoc analysis of the phase 3 clinical trials and open-label extension studies was conducted to evaluate long-term chang...

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Detalles Bibliográficos
Autores principales:	Bichet, Daniel G., Torra, Roser, Wallace, Eric, Hughes, Derralynn, Giugliani, Roberto, Skuban, Nina, Krusinska, Eva, Feldt-Rasmussen, Ulla, Schiffmann, Raphael, Nicholls, Kathy
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Elsevier 2021
Materias:	Research Paper
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8353473/ https://www.ncbi.nlm.nih.gov/pubmed/34401344 http://dx.doi.org/10.1016/j.ymgmr.2021.100786

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